PKAN


Also found in: Medical.
AcronymDefinition
PKANPantothenate Kinase-Associated Neurodegeneration
References in periodicals archive ?
Globus pallidus internus stimulation resulted in significant improvement in BFM outcome scores for patients with DYT1 negative or positive dystonia, PKAN, idiophatic dystonia, tardive dystonia, posttraumatic dystonias, and cerebral palsy.
The SPA (Special Protocol Assessment) indicates concurrence by the US FDA that the design of the pivotal trial can adequately support a New Drug Application (NDA) seeking US approval of RE-024, the company's novel investigational replacement therapy, for the treatment of PKAN.
Globus pallidus hypointensity with or without central hyperintensity is highly characteristic of PKAN (15) (Pantothenate Kinase-Associated Neuropathy) or Hallervorden-Spatz disease.
PKAN is a rare and life-threatening genetic disorder with no approved treatment option.
M2 EQUITYBITES-May 6, 2015-Retrophin passes US FDA's orphan drug designation for RE-024 for PKAN
M2 PHARMA-May 6, 2015-Retrophin passes US FDA's orphan drug designation for RE-024 for PKAN
M2 EQUITYBITES-May 1, 2015-Retrophin to advance RE-024 IND through PKAN clinical development upon US FDA review
M2 PHARMA-May 1, 2015-Retrophin to advance RE-024 IND through PKAN clinical development upon US FDA review